Technologies that can edit genes within the brain have the potential to revolutionize how we treat neurological disorders, and also generate new insights into brain function. To date, attempts to use ...

In a breakthrough, researchers have utilized CRISPR-Cas9 gene editing in mice with a form of Fragile X Syndrome to alter gene expression, resulting in reduction of repetitive behaviors. Fragile X ...

Scientists have used CRISPR-Cas9 gene editing to lessen some autism symptoms in mice with a form of fragile X syndrome, the most common known single-gene cause of autism spectrum disorder. Employing ...

Regions of the genome with repetitive sequences are difficult to selectively edit because it’s hard to control which of the repeated sections will be edited. Ribosomes, the molecular machines that ...

Researchers injected gold nanoparticles (upper right) carrying CRISPR-Cas9 into the brains of mice with fragile X syndrome to edit DNA (scissors) and knock out a neurotransmitter receptor, which ...